Duchenne muscular dystrophy (DMD) is one of the most common Xlinked and lifethreatening childhood diseases and affects about 1 in 3000 newborn boys. Lack of dystrophin protein causes severe progressive muscle wasting and death in the second/third decade of life, due to breathing and circulatory complications. Currently, there are no effective medications for DMD, but many differ ent therapeutic approaches are under active development. In the case of genetic and cell therapies, preclinical and clinical evaluations of safety and validity are paving the way towards effective new therapies which could be available routinely for DMD patients in the next 5 years.
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Feature| June 01 2008
Muscular dystrophy: the route to a cure: Genetic and cell therapies
Taeyoung Koo ;
Takis Athanasopoulos ;
Biochem (Lond) (2008) 30 (3): 18–21.
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Taeyoung Koo, Takis Athanasopoulos, George Dickson; Muscular dystrophy: the route to a cure: Genetic and cell therapies. Biochem (Lond) 1 June 2008; 30 (3): 18–21. doi: https://doi.org/10.1042/BIO03003018
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